Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
IJMS | Free Full-Text | Hepatocellular Carcinoma in β-Thalassemia Patients: Review of the Literature with Molecular Insight into Liver Carcinogenesis
Frontiers | New Insights Into Pathophysiology of β-Thalassemia
Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering the Expression of α-Globin Gene
PDF) Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm
Plasma proteome profiling combined with clinical and genetic features reveals the pathophysiological characteristics of β-thalassemia - ScienceDirect
Β-Thalassemias | NEJM
Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library
β-Thalassemia | Genetics in Medicine
PDF) Cure for thalassemia major – From allogeneic hematopoietic stem cell transplantation to gene therapy
Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu
Thalassemia Reports | Free Full-Text | CRISPR Gene Therapy: A Promising One-Time Therapeutic Approach for Transfusion-Dependent β-Thalassemia—CRISPR-Cas9 Gene Editing for β-Thalassemia
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Survival and complications in patients with haemoglobin E thalassaemia in Sri Lanka: a prospective, longitudinal cohort study - The Lancet Global Health
Gene therapies for transfusion dependent β‐thalassemia: Current status and critical criteria for success - Soni - 2020 - American Journal of Hematology - Wiley Online Library
Pediatric Thalassemia: Practice Essentials, Background, Pathophysiology
Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library
Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Blood Demand and Challenges for Patients With Beta-Thalassemia Major in Eastern Saudi Arabia | Article - Cureus
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
IJMS | Free Full-Text | Thalassemia Intermedia: Chelator or Not?
Guidelines for the Management of Non-Transfusion Dependent Thalassaemias (2nd edition - 2017) by Thalassaemia International Federation (TIF) - Issuu
Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports
Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica
